REGENXBIO, Inc.

Pioneering A New Platform To Treat Diseases

About this Event

Regenxbio [NASDAQ: RGNX] is innovating what is possible in gene therapy with the goal of delivering one-time treatments to patients living with common and rare diseases. The company has three assets in pivotal trials that are set to reach critical milestones this year.

The company is currently targeting Hunter Syndrome, Duchenne Muscular Dystrophy, and Chronic Retinal Disease with treatments that have the potential to become standard of care in markets worth a total of $26B.

In addition to its three late-stage clinical assets, Regenxbio is differentiated from other gene therapy companies in several ways:
  • They are one of a few gene therapy companies worldwide with a cGMP facility capable of producing at commercial scale.
  • They already have partnerships in place with global pharmaceutical companies including Abbvie and Nippon Shinyaku.
  • Their NAV Platform technology is capable of developing broad applications across multiple disease, creating a robust pipeline of future opportunities.

Regenxbio has multiple revenue streams currently in place including milestone payments and licensing deals.

Watch our Fireside Chat with Regenxbio CFO, Mitchell Chanto learn more about Regenxbio’s unique approach to gene therapy and the opportunity this is creating for investors.

Video On Demand

– Recorded

July 24

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